Q&A

Chair(s)

• 

  Ahmar U. Zaidi, MD (he/him/his)

  Medical Director
  Agios Pharmaceuticals
  Troy, Michigan, United States

Speaker(s)

• 

  Yang Dai, MD, PhD (he/him/his)

  Senior Medical Director
  Alexion, AstraZeneca Rare Disease
  Boston, Massachusetts, United States
• 

  Adam Wufsus, PhD (he/him/his)

  Medical Director, Rare Blood Disorders
  Novo Nordisk, Inc.
  Plainsboro, New Jersey, United States
• 

  Ben Hsu, MD, PhD (he/him/his)

  Vice President, Clinical Sciences
  Sangamo Therapeutics
  Brisbane, California, United States
• 

  Sarah Gheuens, MD, PhD (she/her/hers)

  Head of R&D and Chief Medical Officer
  Agios Pharmaceuticals
  Cambridge, Massachusetts, United States
• SM

  Suvankar Majumdar, MD (he/him/his)

  Presenter
  Asklepion Pharmaceuticals
  Children's National Hospital
  Washington, District of Columbia, United States

  Slides
• 

  Valerie Cachat, MSN, APRN, CPNP (she/her/hers)

  Medical Director
  Pfizer
  Avon, Ohio, United States
• 

  Paul Shore, MD, MS

  Clinical Program Director
  CSL Behring
  King of Prussia, Pennsylvania, United States